Clinical Study for Treatment-naïve IOPD Babies to Evaluate Efficacy and Safety of ERT With Avalglucosidase Alfa
Clinical Study for Treatment-naïve IOPD Babies to Evaluate Efficacy and Safety of ERT With Avalglucosidase Alfa
Active, not recruiting · NCT04910776 · Registry updated 2026-04-08Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Clinical Study for Treatment-naïve IOPD Babies to Evaluate Efficacy and Safety of ERT With Avalglucosidase Alfa | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorder | Active, not recruiting | Phase 3 | 2026-04-08 | NCT04910776 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Sanofi | 254 |
6 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Advanced Medical Genetics- Site Number : 8400002 | Hawthorne | United States | 2 |
| Children's Hospitals and Clinics of Minnesota- Site Number : 8400008 | Minneapolis | United States | 1 |
| Cincinnati Children's Hospital Medical Center- Site Number : 8400001 | Cincinnati | United States | 2 |
| Duke University Medical Center- Site Number : 8400004 | Durham | United States | 2 |
| Seattle Children's Hospital- Site Number : 8400003 | Seattle | United States | 2 |
| Stanford Hospital- Site Number : 8400006 | Stanford | United States | 1 |