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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Long-Term Follow-up of Subjects Who Were Treated With ST-920Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry Disease, Cardiac Variant, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorderActive, not recruitingNot stated2026-08-20NCT05039866

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OrganizationsLinked trials
Sangamo Therapeutics5

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Research sitesCityCountryLinked trials
Addenbrooke's HospitalCambridgeUnited Kingdom40
Cincinnati Children's Hospital Medical CenterCincinnatiUnited States405
Emory University School of MedicineAtlantaUnited States47
Lysosomal & Rare Disorders Research & Treatment Center (LDRTC)FairfaxUnited States1
M.A.G.I.C. Clinic Ltd.CalgaryCanada1
Mt. Sinai HospitalNew YorkUnited States2
Royal Free HospitalLondonUnited Kingdom24
The Royal Melbourne HospitalParkvilleAustralia26
University Hospital of WürzburgWürzburgGermany5
University of California, IrvineIrvineUnited States32
University of Iowa Hospital and ClinicsIowa CityUnited States30
University of Minnesota Medical CenterMinneapolisUnited States21
University of South FloridaTampaUnited States33