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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and PediatricsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hyperammonemia, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, methylmalonic acidemia, propionic acidemiaRecruitingNot stated2025-04-15NCT05040178

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OrganizationsLinked trials
RECORDATI GROUP16
Target PharmaSolutions, Inc.10

5 results · Page 1 of 1

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Research sitesCityCountryLinked trials
Ann & Robert H. Lurie Children's Hospital of ChicagoChicagoUnited States144
Children's National HospitalWashington D.C.United States100
Icahn School of Medicine at Mt. SinaiNew YorkUnited States13
Riley Children's HospitalIndianapolisUnited States17
University of South FloridaTampaUnited States65