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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Halting Ornithine Transcarbamylase Deficiency With Recombinant AAV in ChildrEnBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, ornithine carbamoyltransferase deficiency, urea cycle disorderRecruitingPhase 1 / Phase 22023-11-07NCT05092685

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OrganizationsLinked trials
University College, London222

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Research sitesCityCountryLinked trials
Great Ormond Street HospitalLondonUnited Kingdom38