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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Gene Therapy Study of BMN 331 in Subjects With Hereditary AngioedemaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderActive, not recruitingPhase 1 / Phase 22024-05-16NCT05121376

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OrganizationsLinked trials
BioMarin Pharmaceutical32

16 results · Page 1 of 1

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Research sitesCityCountryLinked trials
AARA Research CenterDallasUnited States4
AllerVie Clinical ResearchBirminghamUnited States14
Asthma & Allergy Associates P.C.Colorado SpringsUnited States1
Dr. Henry J. Kanarek Allergy, Asthma & ImmunologyOverland ParkUnited States1
Duke HealthDurhamUnited States3
Hospital Universitario La PazMadridSpain75
Hospital Universitario Vall d'HebronBarcelonaSpain27
Institute For Asthma & AllergyChevy ChaseUnited States1
Medical Research of ArizonaScottsdaleUnited States4
Mississippi Center for Advanced MedicineMadisonUnited States7
Optimed Research, LTDColumbusUnited States2
Royal Prince Alfred Hospital,CamperdownAustralia1
The Pennsylvania State University (Penn State) Milton S. Hershey Medical CenterHersheyUnited States1
University of California San DiegoSan DiegoUnited States3
University of Cincinnati (UC) Physicians Company, LLCCincinnatiUnited States2
Washington University School of MedicineSt LouisUnited States7