Gene Therapy for IGHMBP2-Related Diseases
Gene Therapy for IGHMBP2-Related Diseases
Enrolling by invitation · NCT05152823 · Registry updated 2025-09-30Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Gene Therapy for IGHMBP2-Related Diseases | Charcot-Marie-Tooth disease axonal type 2S, autosomal recessive distal spinal muscular atrophy 1 | Enrolling by invitation | Phase 1 / Phase 2 | 2025-09-30 | NCT05152823 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Megan Waldrop | 1 |
1 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Nationwide Children's Hospital | Columbus | United States | 309 |