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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Intravitreal ERT to Prevent Retinal Disease Progression in Children With CLN2Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Neuronal Ceroid-Lipofuscinoses, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, lysosomal lipid storage disorder, metabolic disease, nervous system disorder, neurodegenerative disease, neuronal ceroid lipofuscinosis 2Active, not recruitingPhase 1 / Phase 22026-04-30NCT05152914

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OrganizationsLinked trials
David L Rogers, MD1

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Research sitesCityCountryLinked trials
Nationwide Children's HospitalColumbusUnited States309