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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Long-term Follow-up Study of Risdiplam in Participants With Spinal Muscular Atrophy (SMA)central nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyActive, not recruitingPhase 42026-09-09NCT05232929

1 results · Page 1 of 1

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OrganizationsLinked trials
Genentech, Inc.221

38 results · Page 1 of 2

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Research sitesCityCountryLinked trials
Advent Health OrlandoWinter ParkUnited States1
All Children's Research Institute, Inc.St. PetersburgUnited States1
Barrow Neurological InstitutePhoenixUnited States50
Central Texas Neurology ConsultantsRound RockUnited States12
Children's Hospital Los AngelesLos AngelesUnited States1
Children's National HospitalWashington D.C.United States100
Childrens Hospital Of PhiladelphiaPhiladelphiaUnited States18
Childrens Hospital of WisconsinMilwaukeeUnited States1
Cincinnati Childrens HospitalCincinnatiUnited States9
Columbia University Med CenterNew YorkUnited States1
Gillette Children's Specialty HealthcareMinnetonkaUnited States1
Helen DeVos Children's Hospital at Spectrum HealthGrand RapidsUnited States27
Instituto de Rehabilitación del CaribeSanturcePuerto Rico1
Loma Linda University Health CareLoma LindaUnited States1
Massachusetts General HospitalBostonUnited States1015
Mayo ClinicRochesterUnited States664
MedStar Georgetown University HospitalWashington D.C.United States204
Methodist Children's Hospital of South TexasSan AntonioUnited States65
Multicare Health System Institute for Research and InnovationTacomaUnited States5
Nemour's Children's Hospital, FloridaOrlandoUnited States1
Neurology & Neuromuscular Care CenterDentonUnited States1
Norton Children's HospitalLouisvilleUnited States79
NYU Hospital for Joint DiseasesNew YorkUnited States3
Penn State Milton S. Hershey Medical CenterHersheyUnited States44
Phoenix Children's HospitalPhoenixUnited States95