A Study to Evaluate the Effect of Venglustat Tablets on Left Ventricular Mass Index in Male and Female Adult Participants With Fabry Disease
A Study to Evaluate the Effect of Venglustat Tablets on Left Ventricular Mass Index in Male and Female Adult Participants With Fabry Disease
Active, not recruiting · NCT05280548 · Registry updated 2026-06-24Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study to Evaluate the Effect of Venglustat Tablets on Left Ventricular Mass Index in Male and Female Adult Participants With Fabry Disease | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorder | Active, not recruiting | Phase 3 | 2026-06-24 | NCT05280548 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Sanofi | 254 |
8 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Ann & Robert H. Lurie Children's Hospital of Chicago- Site Number : 8400005 | Chicago | United States | 1 |
| Emory University School of Medicine - Atlanta- Site Number : 8400009 | Atlanta | United States | 1 |
| Lysosomal and Rare Disorders Research and Treatment Center (LDRTC)- Site Number : 8400004 | Fairfax | United States | 1 |
| Maryam Banikazemi, MD- Site Number : 8400001 | Hawthorne | United States | 1 |
| Renal Disease Research Institute- Site Number : 8400012 | Dallas | United States | 1 |
| University of Alabama -The Kirklin Clinic- Site Number : 8400010 | Birmingham | United States | 1 |
| University of California Los Angeles Medical Center- Site Number : 8400008 | Los Angeles | United States | 1 |
| University of Utah Health Hospital- Site Number : 8400006 | Salt Lake City | United States | 1 |