Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Severe Sickle Cell Disease (SCD)
Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Severe Sickle Cell Disease (SCD)
Active, not recruiting · NCT05329649 · Registry updated 2026-07-01Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Severe Sickle Cell Disease (SCD) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell disease | Active, not recruiting | Phase 3 | 2026-07-01 | NCT05329649 |
2 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| CRISPR Therapeutics | 6 |
| Vertex Pharmaceuticals Incorporated | 37 |
7 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| IRCSS Ospedale Pediatrico Bambino Gesu - Dipartimento di Onco-Ematologia e Terapia Cellulare e Genica | Rome | Italy | 4 |
| Levine Children's Hospital - Hematology | Charlotte | United States | 3 |
| St. Jude Children's Research Hospital | Memphis | United States | 194 |
| St.Mary's Hospital - Haematology Dept | London | United Kingdom | 1 |
| The Children's Hospital of Philadelphia - Hematology | Philadelphia | United States | 2 |
| TriStar Medical Group Children's Specialists - Pediatric Oncology | Nashville | United States | 4 |
| University Hospital Duesseldorf - Department of Pediatric Oncology, Hematology and Clinical Immunology | Düsseldorf | Germany | 2 |