Clinical Study of DTX301 AAV-Mediated Gene Transfer for Ornithine Transcarbamylase (OTC) Deficiency | ClinicalTrials HQ

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Trial	Conditions	Status	Phase	Updated	More info	NCT ID
Clinical Study of DTX301 AAV-Mediated Gene Transfer for Ornithine Transcarbamylase (OTC) Deficiency	Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, ornithine carbamoyltransferase deficiency, urea cycle disorder	Active, not recruiting	Phase 3	2026-09-09		NCT05345171

1 results · Page 1 of 1

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Organizations	Linked trials
Ultragenyx Pharmaceutical Inc	24

16 results · Page 1 of 1

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Research sites	City	Country	Linked trials
Ann & Robert H. Lurie Children's Hospital of Chicago	Chicago	United States	144
Centro Hospitalar Universitario de Sao Joao	Porto	Portugal	3
Clinica Universitaria Reina Fabiola	Córdoba	Argentina	1
Erasmus Universitair Medisch Centrum Rotterrdam	Rotterdam	Netherlands	1
Fujita Health University Hospital	Toyoake	Japan	14
Fundacio Hospital Universitari Vall D'Hebron-Institute de Recerca	Barcelona	Spain	1
Hopital Femme Mere Enfant	Bron	France	1
Hospital de Clinicas de Porto Alegre	Porto Alegre	Brazil	25
Hospital Italiano de Buenos Aires	Buenos Aires	Argentina	7
Kumamoto University Hospital	Kumamoto	Japan	45
Necker-Enfants Maladas Hospital	Paris	France	1
The Hospital For Sick Children	Toronto	Canada	94
Universitatsklinikum Heidelberg	Heidelberg	Germany	7
University Hospitals Cleveland Medical Center	Cleveland	United States	234
University of California	Los Angeles	United States	11
University of Colorado	Aurora	United States	147