Gene Therapy for Adenosine Deaminase Severe Combined Immune Deficiency Using Peripheral Blood and EFS ADA Vector
Gene Therapy for Adenosine Deaminase Severe Combined Immune Deficiency Using Peripheral Blood and EFS ADA Vector
Active, not recruiting · NCT05432310 · Registry updated 2026-08-20Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Gene Therapy for Adenosine Deaminase Severe Combined Immune Deficiency Using Peripheral Blood and EFS ADA Vector | severe combined immunodeficiency, autosomal recessive, T cell-negative, B cell-negative, NK cell-negative, due to adenosine deaminase deficiency | Active, not recruiting | Phase 1 / Phase 2 | 2026-08-20 | NCT05432310 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| University of California, Los Angeles | 355 |
1 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| University of California, Los Angeles (UCLA) | Los Angeles | United States | 14 |