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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Gene Therapy for Cardiomyopathy Associated With Friedreich's AtaxiaCardiomyopathies, Secondary, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Friedreich ataxia, Nutritional and Metabolic Diseases, Spinocerebellar Degenerations, brain disorder, cardiomyopathy, cardiovascular disorder, central nervous system disorder, cerebellar disorder, heart disorder, hereditary disease, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, spinal cord disorderActive, not recruitingPhase 1 / Phase 22025-12-23NCT05445323

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OrganizationsLinked trials
Lexeo Therapeutics7

3 results · Page 1 of 1

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Research sitesCityCountryLinked trials
Ataxia Center and HD Center of Excellence, University of CaliforniaLos AngelesUnited States1
Mayo ClinicRochesterUnited States664
University of South FloridaTampaUnited States73