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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Global, Multicenter Study to Assess Maternal, Fetal and Infant Outcomes of Exposure to Palynziq® (Pegvaliase) During Pregnancy and BreastfeedingBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases and Pregnancy Complications, Nutritional and Metabolic Diseases, Urogenital Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, maternal phenylketonuria, metabolic disease, nervous system disorder, phenylketonuria, pregnancy disorderRecruitingNot stated2026-03-24NCT05579548

2 results · Page 1 of 1

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OrganizationsLinked trials
BioMarin Pharmaceutical32
Syneos Health17

4 results · Page 1 of 1

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Research sitesCityCountryLinked trials
Metabolics and Genetics in Calgary (MAGIC)CalgaryCanada1
Ospedale San PaoloMilanItaly2
Syneos HealthWilmingtonUnited States1
Universitaetsklinikum Hamburg EppendorfHamburgGermany14