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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Evaluation of Intravenous Laronidase Pharmacokinetics Before and After Hematopoietic Cell Transplantation in Patients With Mucopolysaccharidosis Type IH.Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis I, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosisActive, not recruitingNot stated2025-10-30NCT05634512

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Research sitesCityCountryLinked trials
University of Minnesota Masonic Cancer CenterMinneapolisUnited States10