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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Mucolipidosis Type IV Natural History StudyBone Diseases, Metabolic, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, bone disorder, brain disorder, central nervous system disorder, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucolipidosis, musculoskeletal system disorder, nervous system disorderActive, not recruitingNot stated2026-04-23NCT05782387

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OrganizationsLinked trials
Massachusetts General Hospital758

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Research sitesCityCountryLinked trials
Massachusetts General HospitalBostonUnited States7