Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 1 Patients
Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 1 Patients
Recruiting · NCT05824169 · Registry updated 2025-07-03Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 1 Patients | central nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophy | Recruiting | Phase 1 / Phase 2 | 2025-07-03 | NCT05824169 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| GeneCradle Inc | 8 |
4 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Bayi Children's Hospital, Seventh Medical Center, PLA general hospital | Beijing | China | 2 |
| Children's Hospital of Soochow University | Suzhou | China | 1 |
| Peking University， First Hospital, Department of Pediatrics | Beijing | China | 2 |
| Shengjing Hospital of China Medical University | Shenyang | China | 29 |