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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Natural History Study of Participants With Sanfilippo Syndrome Type IIICCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis III, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 3CRecruitingNot stated2026-05-12NCT05825131

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Research sitesCityCountryLinked trials
Hospices Civils De LyonBronFrance1
The University of Texas Southwestern Medical CenterDallasUnited States37