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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Safety and Efficacy of Voxzogo for Growth Deficits in MPS IVA and VICongenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis Type IV A, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 4, mucopolysaccharidosis type 6Active, not recruitingPhase 1 / Phase 22026-03-10NCT05845749

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OrganizationsLinked trials
University of California, San Francisco637

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Research sitesCityCountryLinked trials
UCSF Benioff Children's Hospital OaklandOaklandUnited States85