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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Phase 1, Dose Escalation Trial of RP-A601 in Subjects With PKP2 Variant-Mediated Arrhythmogenic Cardiomyopathy (PKP2-ACM)Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Death, Death, Sudden, Death, Sudden, Cardiac, Pathologic Processes, Pathological Conditions, Signs and Symptoms, arrhythmogenic right ventricular cardiomyopathy, cardiac arrest, cardiomyopathy, cardiovascular disorder, congenital heart disease, heart disorderRecruitingPhase 12026-04-16NCT05885412

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OrganizationsLinked trials
Rocket Pharmaceuticals Inc.10

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Research sitesCityCountryLinked trials
Children's Hospital of PhiladelphiaPhiladelphiaUnited States434
Duke UniversityDurhamUnited States160
University of California, San DiegoLa JollaUnited States25