Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 2 Patients
Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 2 Patients
Active, not recruiting · NCT05901987 · Registry updated 2025-07-03Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 2 Patients | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Spinal Muscular Atrophies of Childhood, central nervous system disorder, hereditary disease, inherited neurodegenerative disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophy | Active, not recruiting | Phase 1 / Phase 2 | 2025-07-03 | NCT05901987 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| GeneCradle Inc | 8 |
5 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Bayi Children's Hospital, Seventh Medical Center, PLA general hospital | Beijing | China | 2 |
| Children's Hospital of Chongqing Medical University | Chongqing | China | 7 |
| Peking University， First Hospital, Department of Pediatrics | Beijing | China | 2 |
| Tongji Medical college of Huazhong University of Science&Technology, Affiliated Children's Hospital | Wuhan | China | 1 |
| West China Second University Hospital, Sichuan University | Chengdu | China | 7 |