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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical StudyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseEnrolling by invitationPhase 32026-02-06NCT05967351

2 results · Page 1 of 1

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OrganizationsLinked trials
Hoffmann-La Roche280
Sarepta Therapeutics, Inc.15

38 results · Page 1 of 2

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Research sitesCityCountryLinked trials
Ann & Robert H. Lurie Children's Hospital of ChicagoChicagoUnited States144
Arkansas Children's HospitalLittle RockUnited States82
Boston Children's HospitalBostonUnited States343
Chiildren's Hospital of PhiladelphiaPhiladelphiaUnited States1
Children's Health Specialty CenterDallasUnited States1
Children's Hospital of ColoradoAuroraUnited States1
Children's Hospital of The King's DaughtersNorfolkUnited States7
Children's Hospital WisconsinMilwaukeeUnited States3
Columbia University Pediatric Neuromuscular CenterNew YorkUnited States3
Great Ormond Street Hospital For Children NHS Foundation TrustLondonUnited Kingdom1
Hong Kong Children's HospitalHong KongHong Kong13
Hospital Sant Joan de DeuEsplugues de LlobregatSpain6
Hospital Universitario y Politecnico La fe. Neurology DepartmentValenciaSpain1
Institute of Translational and Clinical ResearchNewcastle upon TyneUnited Kingdom1
Kaohsiung Medical University Chung-Ho Memorial HospitalKaohsiung CityTaiwan77
Kobe University HospitalKobeJapan28
Lenox Baker Children's Hospital (Duke University)DurhamUnited States2
Lucile Packard Children's Hospital Stanford (LPCH)Palo AltoUnited States1
National Center of Neurology and PsychiatryKodairaJapan12
National Taiwan University HospitalTaipeiTaiwan52
Nationwide Children's HospitalColumbusUnited States309
Oregon Health and Science UniversityPortlandUnited States382
Oxford University Hospitals NHS Foundation TrustOxfordUnited Kingdom7
Rady Children's HospitalSan DiegoUnited States52
The Johns Hopkins Hospital, Rubenstein Child Health BldgBaltimoreUnited States1