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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, X-linked disease, blood coagulation disease, coagulation protein disease, hematologic disorder, hemophilia B, hemorrhagic disease, hereditary disease, inherited blood coagulation disorderRecruitingPhase 32026-08-27NCT06003387

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OrganizationsLinked trials
CSL Behring25

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Research sitesCityCountryLinked trials
Centro de Investigacion Clinica GRAMEL S.C.Mexico CityMexico1
Changhua Christian Hospital (CCH)Chang-huaTaiwan1
Ege University Medical FacultyBornovaTurkey (Türkiye)1
Gaziantep University Sahinbey Research and Practice HospitalGaziantepTurkey (Türkiye)1
Haemophilia Comprehensive Care CentreJohannesburgSouth Africa1
Hemophilia Center of Western Pennsylvania (HCWP)PittsburghUnited States1
Hospital das Clínicas da Faculdade de Medicina da Universidade de São PauloSão PauloBrazil2
Kaohsiung Medical University Chung-Ho Memorial Hospital (KMUH)Kaohsiung CityTaiwan1
King Faisal Specialist Hospital and Research CenterRiyadhSaudi Arabia1
Klinika Zaburzen Hemostazy i Chorob WewnetrznychWarsawPoland1
Kyung Hee University Hospital at GangdongSeoulSouth Korea20
Kyungpook National University HospitalDaeguSouth Korea44
McMaster University - HamiltonHamiltonCanada1
National Taiwan University HospitalTaipeiTaiwan52
National University HospitalSingaporeSingapore1
Prince of Wales Hospital Chinese University of Hong KongShatinHong Kong1
Queen Mary HospitalHong KongHong Kong16
Royal Adelaide HospitalAdelaideAustralia132
Royal Brisbane HospitalHerstonAustralia1
Royal Prince Alfred HospitalCamperdownAustralia83
Severance Hospital, Yonsei University Health SystemSeoulSouth Korea21
Sheba Medical CenterTel LitwinskyIsrael8
Singapore General HospitalSingaporeSingapore48
Specialized Hospital for Active Treatment of Hematological DiseasesSofiaBulgaria1
Taichung Veterans General Hospital -TaichungTaiwan1