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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Shwachman Diamond Syndrome Registry and StudyBone Marrow Failure Disorders, Congenital Bone Marrow Failure Syndromes, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cytopenia, Digestive System Diseases, Hemic and Lymphatic Diseases, Infant, Newborn, Diseases, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Neoplasms by Histologic Type, Nutritional and Metabolic Diseases, Shwachman-Diamond syndrome, agranulocytosis, bone marrow disorder, exocrine pancreatic insufficiency, hematologic disorder, leukemia, leukocyte disorder, leukopenia, lipomatosis, metabolic disease, neoplasm, neutropenia, pancreas disorderRecruitingNot stated2026-04-06NCT06056908

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Research sitesCityCountryLinked trials
Boston Children's HospitalBostonUnited States343
Children's Hospital ColoradoAuroraUnited States312
Cincinnati Children's Hospital Medical CenterCincinnatiUnited States405
Dana-Farber Cancer InstituteBostonUnited States68