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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Phase I/II Study of JR-441 in Patients With Mucopolysaccharidosis Type IIIACongenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis III, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosisActive, not recruitingPhase 1 / Phase 22026-09-04NCT06095388

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OrganizationsLinked trials
JCR Pharmaceuticals Co., Ltd.8

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Research sitesCityCountryLinked trials
Universitätsklinikum Hamburg-EppendorfHamburgGermany31