German Observational Multicenter Study of Patients With Fabry Disease Under Enzyme Replacement Therapy With Pegunigalsidase-alfa
German Observational Multicenter Study of Patients With Fabry Disease Under Enzyme Replacement Therapy With Pegunigalsidase-alfa
Active, not recruiting · NCT06095713 · Registry updated 2026-04-30Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| German Observational Multicenter Study of Patients With Fabry Disease Under Enzyme Replacement Therapy With Pegunigalsidase-alfa | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorder | Active, not recruiting | Not stated | 2026-04-30 | NCT06095713 |
2 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Chiesi GmbH | 1 |
| Universität Münster | 22 |
8 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Fabry disease center Berlin - Charité - Universitätsmedizin Berlin | Berlin | Germany | 1 |
| Fabry disease center Cologne, Universitätsklinikum Köln | Cologne | Germany | 1 |
| Fabry disease center Hamburg, Universitätsklinikum Hamburg | Hamburg | Germany | 1 |
| Fabry disease center Hannover, Universitätsklinikum Hannover | Hanover | Germany | 1 |
| Fabry disease center Mainz, Universitätsmedizin Mainz | Mainz | Germany | 1 |
| Fabry disease center Münster, Universitätsklinikum Münster | Münster | Germany | 1 |
| Fabry disease center Würzburg, Universitätsklinikum Würzburg | Würzburg | Germany | 1 |
| Fachinternistische Gemeinschaftspraxis, Müllheim | Müllheim | Germany | 1 |