Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)
Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)
Recruiting · NCT06150716 · Registry updated 2025-12-12Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD) | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Central Nervous System Demyelinating Diseases, Leukoencephalopathies, Nutritional and Metabolic Diseases, Pelizaeus-Merzbacher spectrum disorder, X-linked disease, brain disorder, central nervous system disorder, demyelinating disease, hereditary disease, inborn errors of metabolism, metabolic disease, nervous system disorder | Recruiting | Phase 1 | 2025-12-12 | NCT06150716 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Ionis Pharmaceuticals, Inc. | 22 |
0 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| No products are listed yet. | |||