Danon Disease Natural History Study
Danon Disease Natural History Study
Recruiting · NCT06214507 · Registry updated 2026-07-28Clinical trials
Swipe the table sideways for more columns.
| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Danon Disease Natural History Study | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Danon disease, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, X-linked disease, cardiomyopathy, cardiovascular disorder, disorder of glycogen metabolism, heart disorder, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, intellectual disability, metabolic disease, nervous system disorder | Recruiting | Not stated | 2026-07-28 | NCT06214507 |
1 results · Page 1 of 1
Organizations
Swipe the table sideways for more columns.
| Organizations | Linked trials |
|---|---|
| Rocket Pharmaceuticals Inc. | 10 |
15 results · Page 1 of 1
Research sites
Swipe the table sideways for more columns.
| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Azienda Ospedaliera Universitaria Meyer IRCCS | Florence | Italy | 7 |
| Children's Hospital Colorado | Aurora | United States | 312 |
| Columbia University Medical Center/New York Presbyterian | New York | United States | 2 |
| German Heart Center Munich | München | Germany | 1 |
| Hospital Universitario Puerta de Hierro Majadahonda | Majadahonda | Spain | 2 |
| Phoenix Children's Hospital | Phoenix | United States | 95 |
| Sant Joan de Déu Hospital | Barcelona | Spain | 1 |
| Sheba Medical Center | Ramat Gan | Israel | 11 |
| Texas Children's Hospital | Houston | United States | 187 |
| University College London - Great Ormond Street Institute of Child Health | London | United Kingdom | 1 |
| University of California, San Diego | La Jolla | United States | 25 |
| University of Florida College of Medicine | Gainesville | United States | 14 |
| University of Michigan | Ann Arbor | United States | 538 |
| University of Texas, Southwestern | Dallas | United States | 4 |
| Washington University | St Louis | United States | 182 |