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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Screening for Gaucher Disease and Acid Sphingomyelinase DeficiencyBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gaucher disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosisNot yet recruitingNot stated2024-04-15NCT06258577

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OrganizationsLinked trials
Chung-Hsing Wang1
Sanofi254

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Research sitesCityCountryLinked trials
China Medical University HospitaTaichungTaiwan1