Screening for Gaucher Disease and Acid Sphingomyelinase Deficiency
Screening for Gaucher Disease and Acid Sphingomyelinase Deficiency
Not yet recruiting · NCT06258577 · Registry updated 2024-04-15Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Screening for Gaucher Disease and Acid Sphingomyelinase Deficiency | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gaucher disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis | Not yet recruiting | Not stated | 2024-04-15 | NCT06258577 |
2 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Chung-Hsing Wang | 1 |
| Sanofi | 254 |
1 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| China Medical University Hospita | Taichung | Taiwan | 1 |