A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy
A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy
Active, not recruiting · NCT06280209 · Registry updated 2026-06-25Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Active, not recruiting | Phase 1 / Phase 2 | 2026-06-25 | NCT06280209 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| BioMarin Pharmaceutical | 32 |
7 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Fondazione Serena ETS - Centro Clinico NeMO Milano | Milan | Italy | 3 |
| Great Ormond Street Hospital NHS Foundation Trust | London | United Kingdom | 3 |
| Hospital Sant Joan de Deu | Barcelona | Spain | 11 |
| Hospital Viamed Santa Angela De la Cruz | Seville | Spain | 1 |
| Leids Universitair Medisch Centrum | Leiden | Netherlands | 29 |
| UOC Fase I - Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore | Rome | Italy | 1 |
| Yeditepe University Kosuyolu Hospital | Istanbul | Turkey (Türkiye) | 2 |