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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuriaRecruitingNot stated2026-03-24NCT06305234

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OrganizationsLinked trials
BioMarin Pharmaceutical32

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Research sitesCityCountryLinked trials
Boston Children's HospitalBostonUnited States20
Children's Wisconsin/Medical College of WisconsinMilwaukeeUnited States3
Emory UniversityAtlantaUnited States262
Northwestern UniversityChicagoUnited States727
Oregon Health & Science UniversityPortlandUnited States261
Riley Children's Hospital/ Indiana University HealthIndianapolisUnited States1
Tulane University School of MedicineNew OrleansUnited States47
University of ColoradoAuroraUnited States147
University of Pittsburgh Medical CenterPittsburghUnited States127
UT Southwestern Medical CenterDallasUnited States210
Vanderbilt University Medical SchoolNashvilleUnited States2