Single Participant Study of an Experimental ASO Treatment for TUBB4A-related Leukodystrophy
Single Participant Study of an Experimental ASO Treatment for TUBB4A-related Leukodystrophy
Enrolling by invitation · NCT06369974 · Registry updated 2026-03-02Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Single Participant Study of an Experimental ASO Treatment for TUBB4A-related Leukodystrophy | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, hereditary disease | Enrolling by invitation | Phase 1 / Phase 2 | 2026-03-02 | NCT06369974 |
2 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Massachusetts General Hospital | 758 |
| n-Lorem Foundation | 18 |
1 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Massachusetts General Hospital | Boston | United States | 1015 |