Evaluation of the Safety and Efficacy of Late-onset Pompe Disease Gene Therapy Drug
Evaluation of the Safety and Efficacy of Late-onset Pompe Disease Gene Therapy Drug
Recruiting · NCT06391736 · Registry updated 2025-07-03Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Evaluation of the Safety and Efficacy of Late-onset Pompe Disease Gene Therapy Drug | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorder | Recruiting | Phase 1 / Phase 2 | 2025-07-03 | NCT06391736 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| GeneCradle Inc | 8 |
1 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Chinese PLA General Hospital | Beijing | China | 13 |