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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
An Observational Study in Subjects to Follow the Progression of Stargardt Disease Type 1 (STGD1) Caused by Bi-Allelic Autosomal Recessive Mutations in the ABCA4 GeneCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Hereditary, Stargardt disease, eye disorder, hereditary disease, macular degeneration, retinal degeneration, retinal disorderRecruitingNot stated2025-09-19NCT06435000

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OrganizationsLinked trials
Splice Bio2

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Research sitesCityCountryLinked trials
Bascom Palmer Eye InstituteMiamiUnited States17
Columbia University Medical centerNew YorkUnited States224
CUIMC/Edward S. Harkness Eye InstituteNew YorkUnited States1
Duke Eye CenterDurhamUnited States14
Emory UniversityAtlantaUnited States262
Kellogg Clinical Research CenterAnn ArborUnited States1
Leeds Teaching Hospitals NHS TrustLeedsUnited Kingdom1
Massachusetts Eye and Ear InfirmaryBostonUnited States18
Moorfields Eye HospitalLondonUnited Kingdom2
Oregon Health & Science UniversityPortlandUnited States261
Oxford Eye HospitalOxfordUnited Kingdom2
Retina Foundation of the SouthwestDallasUnited States38
Shiley Eye InstituteSan DiegoUnited States1
UCHealth Sue Anschutz-Rodgers Eye CenterAuroraUnited States2
University Eye Hospital TübingenTübingenGermany1
University of Manchester - The Old St Mary's HospitalManchesterUnited Kingdom1
University of Wisconsin, MadisonMadisonUnited States2
Universitätsklinikum Bonn, Klinik für AugenheilkundeBonnGermany1
Vitreo Retinal AssociatesGainesvilleUnited States10
Wilmer Eye Institute, Johns Hopkins University MD 21287BaltimoreUnited States1