ADAPT Study: Long-term Safety Study of INZ-701 in Patients With ENPP1 Deficiency and ABCC6 Deficiency
ADAPT Study: Long-term Safety Study of INZ-701 in Patients With ENPP1 Deficiency and ABCC6 Deficiency
Active, not recruiting · NCT06462547 · Registry updated 2026-08-28Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| ADAPT Study: Long-term Safety Study of INZ-701 in Patients With ENPP1 Deficiency and ABCC6 Deficiency | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Skin Abnormalities, Skin and Connective Tissue Diseases, arterial calcification of infancy, autosomal recessive inherited pseudoxanthoma elasticum, cardiovascular disorder, connective tissue disorder, hematologic disorder, hemorrhagic disease, hereditary disease, hereditary skin disorder, hypophosphatemic rickets, autosomal recessive, 2, skin disorder, vascular disorder, vascular hemostatic disease | Active, not recruiting | Phase 2 | 2026-08-28 | NCT06462547 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Inozyme Pharma | 2 |
5 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Clinilabs Drug Development Corporation | Eatontown | United States | 3 |
| Mayo Clinic | Rochester | United States | 664 |
| Medical Research Network Ltd. | Milton Keynes | United Kingdom | 1 |
| Necker-Enfants Malades Hospital | Paris | France | 3 |
| Universitätsklinikum Hamburg-Eppendorf (UKE) | Hamburg | Germany | 3 |