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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
ADAPT Study: Long-term Safety Study of INZ-701 in Patients With ENPP1 Deficiency and ABCC6 DeficiencyCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Skin Abnormalities, Skin and Connective Tissue Diseases, arterial calcification of infancy, autosomal recessive inherited pseudoxanthoma elasticum, cardiovascular disorder, connective tissue disorder, hematologic disorder, hemorrhagic disease, hereditary disease, hereditary skin disorder, hypophosphatemic rickets, autosomal recessive, 2, skin disorder, vascular disorder, vascular hemostatic diseaseActive, not recruitingPhase 22026-08-28NCT06462547

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OrganizationsLinked trials
Inozyme Pharma2

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Research sitesCityCountryLinked trials
Clinilabs Drug Development CorporationEatontownUnited States3
Mayo ClinicRochesterUnited States664
Medical Research Network Ltd.Milton KeynesUnited Kingdom1
Necker-Enfants Malades HospitalParisFrance3
Universitätsklinikum Hamburg-Eppendorf (UKE)HamburgGermany3