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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study to Evaluate Safety, Tolerability and Efficacy of Inclisiran in Children With Homozygous Familial HypercholesterolemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Hypercholesterolemia, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, Ventricular Outflow Obstruction, aortic valve disorder, aortic valve stenosis, cardiovascular disorder, familial hypercholesterolemia, heart disorder, heart failure, heart valve disorder, hereditary disease, homozygous familial hypercholesterolemia, hyperlipidemia, hyperlipoproteinemia, inborn errors of metabolism, metabolic diseaseRecruitingPhase 32026-07-24NCT06597006

1 results · Page 1 of 1

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OrganizationsLinked trials
Novartis Pharmaceuticals432

4 results · Page 1 of 1

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Research sitesCityCountryLinked trials
Childrens National HospitalWashington D.C.United States10
Primary Childrens Medical CenterSalt Lake CityUnited States3
UC San Francisco Medical CenterSan FranciscoUnited States3
Washington Univ School Of MedicineSt LouisUnited States4