A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients
A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients
Recruiting · NCT06663358 · Registry updated 2025-11-14Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorder | Recruiting | Not stated | 2025-11-14 | NCT06663358 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Chiesi Farmaceutici S.p.A. | 24 |
10 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Emory University School of Medicine | Atlanta | United States | 47 |
| General Hospital Slovenj Gradec | Slovenj Gradec | Slovenia | 1 |
| Infusion Associates | Grand Rapids | United States | 3 |
| Lysosomal & Rare Disorder Research & Treatment Center (LRDRTC) | Fairfax | United States | 1 |
| Northwestern University - Feinberg School of Medicine - Ann & Robert H. Lurie Children's Hospital of Chicago | Chicago | United States | 2 |
| Salford Royal | Salford | United Kingdom | 1 |
| The Royal Free Hospital | London | United Kingdom | 3 |
| University Hospitals Birmingham NHS Foundation Trust, Queen Elizabeth Hospital | Edgbaston | United Kingdom | 1 |
| University of Alabama at Birmingham | Birmingham | United States | 247 |
| University of Iowa Hospitals and Clinics | Iowa City | United States | 99 |