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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of Vosoritide in Children With Noonan Syndrome With Inadequate Growth During or After Human Growth Hormone TreatmentBone Diseases, Developmental, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, Dwarfism, Musculoskeletal Abnormalities, Noonan syndrome, Skin and Connective Tissue Diseases, bone disorder, cardiovascular disorder, congenital heart disease, connective tissue disorder, endocrine system disorder, heart disorder, hereditary disease, musculoskeletal system disorderActive, not recruitingPhase 22026-09-23NCT06668805

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OrganizationsLinked trials
BioMarin Pharmaceutical32

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Research sitesCityCountryLinked trials
Angers University Hospital CenterAngersFrance1
Ann & Robert H. Lurie Children's Hospital of ChicagoChicagoUnited States144
Atrium Health Carolinas Medical CenterCharlotteUnited States12
Azienda Ospedaliero Universitaria - Ospedale Pediatrico MeyerFlorenceItaly1
Central University Hospital of AsturiasOviedoSpain2
Centre Hospitalier Universitaire Sainte-JustineMontrealCanada70
Children's Hospital at MontefioreThe BronxUnited States29
Children's Hospital ColoradoAuroraUnited States312
Children's Hospital of Orange County Main Campus - OrangeOrangeUnited States4
Children's Medical Center DallasDallasUnited States18
Children's National Medical CenterWashington D.C.United States177
Childrens Health Queensland Hospital and Health ServiceSouth BrisbaneAustralia1
Childrens Hospital Los AngelesLos AngelesUnited States13
Childrens Hospital Of PhiladelphiaPhiladelphiaUnited States18
CHU de Toulouse - Hôpital des EnfantsToulouseFrance1
Cincinnati Children's Hospital Medical CenterCincinnatiUnited States5
Emory University School of MedicineAtlantaUnited States47
Fondazione Policlinico Universitario Agostino Gemelli IRCCSRomaItaly1
Froedtert & Medical College of WisconsinMilwaukeeUnited States13
Hospital Clínico Universitario de SantiagoSantiago de CompostelaSpain2
Hôpital de la TimoneMarseilleFrance4
Hôpital Robert-DebréParisFrance1
Icahn School of Medicine at Mount SinaiNew YorkUnited States342
IRCCS Istituto Giannina GasliniGenovaItaly1
Kentucky Children's HospitalLexingtonUnited States1