A Phase 3 Study of NTLA-2001 in ATTRv-PN
A Phase 3 Study of NTLA-2001 in ATTRv-PN
Recruiting · NCT06672237 · Registry updated 2026-04-16Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Phase 3 Study of NTLA-2001 in ATTRv-PN | Amyloid Neuropathies, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, amyloidosis, familial amyloid neuropathy, hereditary amyloidosis, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, polyneuropathy, proteostasis deficiencies | Recruiting | Phase 3 | 2026-04-16 | NCT06672237 |
2 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Intellia Therapeutics | 7 |
| Regeneron Pharmaceuticals | 238 |
14 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Chang Gung Medical Foundation - Linkou Branch | Taoyuan | Taiwan | 1 |
| HCFMRP - Hospital das Clinicas da Faculdade de Medicina de Ribeirao Preto | Ribeirão Preto | Brazil | 2 |
| Hospital Británico de Buenos Aires | Buenos Aires | Argentina | 3 |
| Hospital das Clinicas da Universidade Estadual de Campinas (UNICAMP) | Campinas | Brazil | 1 |
| Hospital El Cruce | San Juan Bautista | Argentina | 2 |
| Hospital Italiano de Buenos Aires (HIBA) | Buenos Aires | Argentina | 2 |
| Instituto de Educacao, Pesquisa e Gestao em Saude | Rio de Janeiro | Brazil | 1 |
| National Institute of Medical Sciences and Nutrition - Salvador Zubiran (INCMNSZ) | Tlalpan | Mexico | 1 |
| National Taiwan University Hospital | Taipei | Taiwan | 203 |
| National University Hospital | Singapore | Singapore | 46 |
| PSEG Centro de Pesquisa Clinica S.A. | São Paulo | Brazil | 2 |
| Singapore General Hospital | Singapore | Singapore | 33 |
| Siriraj Hospital | Bangkok | Thailand | 10 |
| Taipei Veterans General Hospital | Taipei | Taiwan | 64 |