Personalized Antisense Oligonucleotide Therapy for A Single Participant With ATN1 Gene Mutation

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Trial	Conditions	Status	Phase	Updated	More info	NCT ID
Personalized Antisense Oligonucleotide Therapy for A Single Participant With ATN1 Gene Mutation	Epilepsies, Myoclonic, Epilepsy, Generalized, Epileptic Syndromes, brain disorder, central nervous system disorder, dentatorubral-pallidoluysian atrophy, epilepsy, nervous system disorder, progressive myoclonus epilepsy	Active, not recruiting	Phase 1 / Phase 2	2026-04-09		NCT06706388

2 results · Page 1 of 1

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Organizations	Linked trials
Columbia University	375
n-Lorem Foundation	18

1 results · Page 1 of 1

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Research sites	City	Country	Linked trials
Columbia University	New York	United States	22

Clinical trials