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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Hyperammonemia, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, X-linked disease, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, liver disorder, metabolic disease, nervous system disorder, ornithine carbamoyltransferase deficiency, urea cycle disorderRecruitingNot stated2026-08-31NCT06805695

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OrganizationsLinked trials
iECURE, Inc.2

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Research sitesCityCountryLinked trials
Children's Hospital of Colorado, Anshutz Medical CampusAuroraUnited States2
Great Ormond Street HospitalLondonUnited Kingdom15
Icahn School of Medicine at Mount SinaiNew YorkUnited States342