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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Sirolimus for Leigh SyndromeBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Leigh syndrome, Nutritional and Metabolic Diseases, Pyruvate Metabolism, Inborn Errors, brain disorder, central nervous system disorder, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, inborn mitochondrial metabolism disorder, metabolic disease, nervous system disorderEnrolling by invitationPhase 22026-03-31NCT06843811

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OrganizationsLinked trials
Matthew Demczko1

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Research sitesCityCountryLinked trials
Children's Hospital of PhiladelphiaPhiladelphiaUnited States22