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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Base-Edited Hematopoietic Stem/Progenitor Cell X-Linked Severe Combined Immunodeficiency Gene TherapyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Infant, Newborn, Diseases, Primary Immunodeficiency Diseases, X-Linked Combined Immunodeficiency Diseases, X-linked disease, hereditary disease, immune system disorder, inborn error of immunity, severe combined immunodeficiencyEnrolling by invitationPhase 1 / Phase 22026-09-23NCT06851767

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Research sitesCityCountryLinked trials
National Institutes of Health Clinical CenterBethesdaUnited States800