Efficacy and Safety of Enzyme Replacement Therapy in Patients With Fabry Disease
Efficacy and Safety of Enzyme Replacement Therapy in Patients With Fabry Disease
Enrolling by invitation · NCT06880250 · Registry updated 2025-12-31Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Efficacy and Safety of Enzyme Replacement Therapy in Patients With Fabry Disease | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorder | Enrolling by invitation | Not stated | 2025-12-31 | NCT06880250 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| NPO Petrovax | 2 |
23 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| #10 | Krasnodar | Russia | 1 |
| #11 | Ufa | Russia | 1 |
| #12 | Ivanovo | Russia | 1 |
| #13 | Astrakhan | Russia | 1 |
| #15 | Orenburg | Russia | 1 |
| #16 | Gubkin | Russia | 1 |
| #17 | Omsk | Russia | 1 |
| #18 | Kurgan | Russia | 1 |
| #19 | Kaa-Khem | Russia | 1 |
| #2 | Rostov-on-Don | Russia | 1 |
| #21 | Grozny | Russia | 1 |
| #22 | Stavropol | Russia | 1 |
| #23 | Polevskoy | Russia | 1 |
| #24 | Ryazan | Russia | 1 |
| #26 | Irkutsk | Russia | 1 |
| #27 | Barnaul | Russia | 1 |
| #3 | Simferopol | Russia | 1 |
| #4 | Rostov-on-Don | Russia | 1 |
| #5 | Voronezh | Russia | 1 |
| #6 | Chelyabinsk | Russia | 1 |
| #7 | Borovichi | Russia | 1 |
| #8 | Saint Petersburg | Russia | 1 |
| #9 | Perm | Russia | 1 |