Safety and Efficacy Evaluation of GC101 Gene Therapy Via Intrathecal (IT) Injectionin the Treatment of Patients With Type 2 Spinal Muscular Atrophy (SMA) - Phase III
Safety and Efficacy Evaluation of GC101 Gene Therapy Via Intrathecal (IT) Injectionin the Treatment of Patients With Type 2 Spinal Muscular Atrophy (SMA) - Phase III
Recruiting · NCT06971094 · Registry updated 2025-06-05Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Safety and Efficacy Evaluation of GC101 Gene Therapy Via Intrathecal (IT) Injectionin the Treatment of Patients With Type 2 Spinal Muscular Atrophy (SMA) - Phase III | central nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophy | Recruiting | Phase 3 | 2025-06-05 | NCT06971094 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| GeneCradle Inc | 8 |
7 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Beijing Children's Hospital, Capital Medical University | Beijing | China | 9 |
| Children's Hospital of Soochow University | Suzhou | China | 7 |
| Children's Medical Center of Peking University First Hospital | Beijing | China | 1 |
| National Children's Medical Center，Shanghai Jiaotong University | Shanghai | China | 1 |
| Shenzhen Children's Hospital | Shenzhen | China | 6 |
| The Seventh Medical Center of Chinese PLA General Hospital | Beijing | China | 1 |
| Wuhan Children's Hospital, Tongji Medical College, Huazhong University of Science & Technology | Wuhan | China | 1 |