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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Evaluate Del-brax (Also Referred to as AOC 1020) in Participants With FSHDCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Disorders, Atrophic, facioscapulohumeral muscular dystrophy, facioscapulohumeral muscular dystrophy 1, facioscapulohumeral muscular dystrophy 2, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingPhase 32026-07-27NCT07038200

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OrganizationsLinked trials
Avidity Biosciences, Inc.6

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Research sitesCityCountryLinked trials
Aarhus University HospitalAarhusDenmark77
Academisch Ziekenhuis LeidenLeidenNetherlands4
AP-HP Hopital Pitie-SalpetriereParisFrance2
Azienda Ospedaliero Universitaria PisanaPisaItaly22
Azienda Ospedaliero-Universitaria Sant'AndreaRomaItaly2
Centre de Reference des Maladies Neuromusculaires et de la SLA - AP-HM Hopital de La TimoneMarseilleFrance2
CHU de Montpellier - Hopital Gui de ChauliacMontpellierFrance1
CHU de Nice - Hopital Pasteur 2 - Centre de reference des Maladies NeuromusculairesNiceFrance2
Duke UniversityDurhamUnited States45
Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro CuoreRomaItaly2
Fondazione Serena ETS - Centro Clinico NeMO MilanoMilanItaly3
Genge Partners IncMontrealCanada1
Georg-August-Universitaet Goettingen Stiftung oeffentlichen Rechts Universitaetsmedizin GoettingenGöttingenGermany1
Hospital Universitari de BellvitgeBarcelonaSpain11
Hospital Universitari i Politecnic La FeValenciaSpain14
Hospital Universitario DonostiaSan SebastiánSpain6
Hospital Universitario Vall d'HebronBarcelonaSpain27
Kansas University Medical CenterKansas CityUnited States3
Kennedy Krieger InstituteBaltimoreUnited States41
Klinikum der Ludwig-Maximilians-Universitaet MuenchenMünchenGermany3
National Center of Neurology and PsychiatryTokyoJapan5
National Hospital for Neurology & NeurosurgeryLondonUnited Kingdom3
National Hospital Organization Osaka Toneyama Medical CenterOsakaJapan1
National Hospital Organization Sendai Nishitaga HospitalSendaiJapan1
Ohio State UniversityColumbusUnited States19