Gene Therapy for Wilson Disease Evaluated by 64Cu PET/CT
Gene Therapy for Wilson Disease Evaluated by 64Cu PET/CT
Enrolling by invitation · NCT07159581 · Registry updated 2025-09-08Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Gene Therapy for Wilson Disease Evaluated by 64Cu PET/CT | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Nutritional and Metabolic Diseases, Wilson disease, basal ganglia disorder, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, inborn metal metabolism disorder, inherited neurodegenerative disorder, liver disorder, metabolic disease, movement disorder, nervous system disorder, neurodegenerative disease | Enrolling by invitation | Not stated | 2025-09-08 | NCT07159581 |
2 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Thomas Damgaard Sandahl | 1 |
| Ultragenyx Pharmaceutical Inc | 24 |
1 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Aarhus University Hospital | Aarhus | Denmark | 5 |