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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of SGT-212 Gene Therapy in Friedreich's AtaxiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Dyskinesias, Friedreich ataxia, Neurologic Manifestations, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, Signs and Symptoms, Spinocerebellar Degenerations, atactic disorder, non-human animal, brain disorder, central nervous system disorder, cerebellar disorder, hereditary disease, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, metabolic disease, movement disorder, nervous system disorder, neurodegenerative disease, spinal cord disorderRecruitingPhase 12026-09-29NCT07180355

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OrganizationsLinked trials
Solid Biosciences Inc.5

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Research sitesCityCountryLinked trials
The Children's Hospital of Philadelphia (CHOP)PhiladelphiaUnited States7
The Ohio State UniversityColumbusUnited States191
The University of California, Los Angeles (UCLA)Los AngelesUnited States1