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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Gaucher Disease Gene Therapy Trial With FLT201Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gaucher Disease, Type 1, Gaucher disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosisRecruitingPhase 32026-09-03NCT07223944

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OrganizationsLinked trials
Spur Therapeutics2

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Research sitesCityCountryLinked trials
Addenbrooke's HospitalCambridgeUnited Kingdom40
Children's Hospital of PhiladelphiaPhiladelphiaUnited States434
Cincinnati Children's Hospital Medical CenterCincinnatiUnited States405
Clinica Universitaria Reina FabiolaCórdobaArgentina1
Columbia UniversityNew YorkUnited States154
Duke University Medical CenterDurhamUnited States505
Emory HealthcareAtlantaUnited States5
Gazi University Medical FacultyAnkaraTurkey (Türkiye)1
Hackensack University Medical CenterHackensackUnited States308
Hospital de Clinicas de Porto AlegrePorto AlegreBrazil25
Hospital Italiano de Buenos AiresBuenos AiresArgentina25
Hospital Militar CentralBuenos AiresArgentina1
Hospital Quironsalud de ZaragozaZaragozaSpain1
Hospital Universitario Vall d'HebronBarcelonaSpain9
Kaiser Permanente - CALos AngelesUnited States1
King Faisal Specialist Hospital and Research CenterRiyadhSaudi Arabia2
Lady Davis Institute for Medical Research Jewish General HospitalMontrealCanada1
Lysosomal Rare Disorders Research and Treatment CenterFairfaxUnited States2
MAGIC Clinic LtdCalgaryCanada1
Melbourne Health - Royal Melbourne HospitalMelbourne N.Australia1
NYU Langone HealthNew YorkUnited States23
Queen Elizabeth Hospital BirminghamBirminghamUnited Kingdom2
Rabin Medical Center, Beilinson HospitalPetah TikvaIsrael4
Royal Free HospitalLondonUnited Kingdom3
Salford Royal HospitalSalfordUnited Kingdom2