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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Prescreening Study to Identify Potential Wilson Disease Participants for Gene-Editing Clinical TrialBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Nutritional and Metabolic Diseases, Wilson disease, basal ganglia disorder, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, inborn metal metabolism disorder, inherited neurodegenerative disorder, liver disorder, metabolic disease, movement disorder, nervous system disorder, neurodegenerative diseaseActive, not recruitingNot stated2026-05-12NCT07226622

1 results · Page 1 of 1

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OrganizationsLinked trials
Prime Medicine, Inc.3

7 results · Page 1 of 1

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Research sitesCityCountryLinked trials
American Research CorporationSan AntonioUnited States7
Massachusetts General HospitalBostonUnited States1015
Northwestern UniversityChicagoUnited States727
University of California Davis HealthSacramentoUnited States15
University of California Los Angeles Medical CenterLos AngelesUnited States2
University of Michigan MedicineAnn ArborUnited States4
Yale New Haven HospitalNew HavenUnited States27